ALS ARSACS ASO Treatment Ataxia Biomarker Cerebellum Function Clinical Trials CRISPR DNA DNA Repair DRPLA Gene Therapy HD IAAD IAAD19 IAAD2019 Ion Channel Knowledge Translation Mouse Models MRI Neuron Oxidative Stress Polyglutamine Diseases Purkinje Cells RAN Translation RNA RNAi SARA Scale SBMA SCA1 SCA2 SCA3 SCA5 SCA6 SCA7 SCA8 SCA12 SCA13 SCA14 SCA17 Special Series: The Discovery Stem cells Website Launch Zebrafish